The partnership aims to accelerate the development of treatments for neurological diseases by providing a cutting-edge biorepository for pediatric CNS tissue and biofluids. The repository will house high-quality, well-characterized human tissues and bio fluids, supporting drug discovery efforts and biomarker identification.
CURE GABA-A and Grann Pharmaceuticals partner to advance mRNA lipid nanoparticle therapies for Rett Syndrome and other rare neurodevelopmental disorders caused by GABAAR variants. The partnership aims to accelerate clinical trials and deliver transformative therapies to families affected by these conditions.
COMBINEDBrain, a non-profit organization, has received a grant from the Chan Zuckerberg Initiative to accelerate research for rare genetic neurodevelopmental disorders. The foundation aims to strengthen patient advocacy groups through collaboration with academia, industry, and clinicians.